{"id":33238,"date":"2024-08-03T15:01:19","date_gmt":"2024-08-03T19:01:19","guid":{"rendered":"https:\/\/avalere.com\/?p=33238"},"modified":"2024-10-03T15:06:25","modified_gmt":"2024-10-03T19:06:25","slug":"clinical-trial-designs-for-rare-and-ultra-rare-disease","status":"publish","type":"post","link":"https:\/\/advisory.avalerehealth.com\/news\/clinical-trial-designs-for-rare-and-ultra-rare-disease","title":{"rendered":"Clinical Trial Designs for Rare and Ultra-Rare Disease"},"content":{"rendered":"<p>When designing <a href=\"https:\/\/advisory.avalerehealth.com\/insights\/decentralized-clinical-trials-for-rare-disease-treatments\">clinical trials<\/a> for rare and ultra-rare diseases, manufacturers must uncover ways to overcome the geographical and ethical challenges that do not plague chronic disease studies. The article by Mariia Saldova, \u201cInnovating Clinical Trial Designs in Rare and Ultra-Rare Disease,\u201d explores the importance of decentralized clinical trials in a patient population that is difficult to find and explains the benefits to patients seeking access to new therapies. The author describes how one gene therapy company was able to recruit and retain patients using innovative recruitment methods. She also discusses the importance of collaborating with advocacy groups and minority communities to identify and <a href=\"https:\/\/advisory.avalerehealth.com\/insights\/ebook-rare-disease-biotechnology-landscape\">reach new patients<\/a>.<\/p>\n<p>To read the complete article, visit Med Ad News\u2019 blog, <a href=\"https:\/\/www.pharmalive.com\/innovating-clinical-trial-designs-in-rare-and-ultra-rare-disease\/\">PharmaLive.com<\/a>.<\/p>\n<p><strong>Learn More<\/strong><br \/>\nTo learn more about how Avalere applies its robust experience in drug development, clinical trial design, and rare disease therapeutics, <a href=\"https:\/\/pages.avalere.com\/Insights.html\">connect with us<\/a>.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>When designing clinical trials for rare and ultra-rare diseases, manufacturers must uncover ways to overcome the geographical and ethical challenges that do not plague chronic disease studies. The article by Mariia Saldova, \u201cInnovating Clinical Trial Designs in Rare and Ultra-Rare Disease,\u201d explores the importance of decentralized clinical trials in a patient population that is difficult&hellip;<\/p>\n","protected":false},"author":35,"featured_media":0,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":""},"categories":[995],"tags":[],"content-categories":[719],"class_list":["post-33238","post","type-post","status-publish","format-standard","hentry","category-news","content-categories-health-equity","entry","no-media"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v24.0 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>Clinical Trial Designs for Rare and Ultra-Rare Disease | Avalere Health Advisory<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/advisory.avalerehealth.com\/news\/clinical-trial-designs-for-rare-and-ultra-rare-disease\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Clinical Trial Designs for Rare and Ultra-Rare Disease | Avalere Health Advisory\" \/>\n<meta property=\"og:description\" content=\"When designing clinical trials for rare and ultra-rare diseases, manufacturers must uncover ways to overcome the geographical and ethical challenges that do not plague chronic disease studies. The article by Mariia Saldova, \u201cInnovating Clinical Trial Designs in Rare and Ultra-Rare Disease,\u201d explores the importance of decentralized clinical trials in a patient population that is difficult&hellip;\" \/>\n<meta property=\"og:url\" content=\"https:\/\/advisory.avalerehealth.com\/news\/clinical-trial-designs-for-rare-and-ultra-rare-disease\" \/>\n<meta property=\"og:site_name\" content=\"Avalere Health Advisory\" \/>\n<meta property=\"article:published_time\" content=\"2024-08-03T19:01:19+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2024-10-03T19:06:25+00:00\" \/>\n<meta name=\"author\" content=\"mgomez@avalere.com\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:creator\" content=\"@avalerehealth\" \/>\n<meta name=\"twitter:site\" content=\"@avalerehealth\" \/>\n<meta name=\"twitter:label1\" content=\"Written by\" \/>\n\t<meta name=\"twitter:data1\" content=\"mgomez@avalere.com\" \/>\n\t<meta name=\"twitter:label2\" content=\"Est. reading time\" \/>\n\t<meta name=\"twitter:data2\" content=\"1 minute\" \/>\n<!-- \/ Yoast SEO plugin. -->","yoast_head_json":{"title":"Clinical Trial Designs for Rare and Ultra-Rare Disease | Avalere Health Advisory","robots":{"index":"index","follow":"follow","max-snippet":"max-snippet:-1","max-image-preview":"max-image-preview:large","max-video-preview":"max-video-preview:-1"},"canonical":"https:\/\/advisory.avalerehealth.com\/news\/clinical-trial-designs-for-rare-and-ultra-rare-disease","og_locale":"en_US","og_type":"article","og_title":"Clinical Trial Designs for Rare and Ultra-Rare Disease | Avalere Health Advisory","og_description":"When designing clinical trials for rare and ultra-rare diseases, manufacturers must uncover ways to overcome the geographical and ethical challenges that do not plague chronic disease studies. The article by Mariia Saldova, \u201cInnovating Clinical Trial Designs in Rare and Ultra-Rare Disease,\u201d explores the importance of decentralized clinical trials in a patient population that is difficult&hellip;","og_url":"https:\/\/advisory.avalerehealth.com\/news\/clinical-trial-designs-for-rare-and-ultra-rare-disease","og_site_name":"Avalere Health Advisory","article_published_time":"2024-08-03T19:01:19+00:00","article_modified_time":"2024-10-03T19:06:25+00:00","author":"mgomez@avalere.com","twitter_card":"summary_large_image","twitter_creator":"@avalerehealth","twitter_site":"@avalerehealth","twitter_misc":{"Written by":"mgomez@avalere.com","Est. reading time":"1 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